My Pathway to Adeno-Associated Virus and Adeno-Associated Virus Gene Therapy: A Personal Perspective
نویسندگان
چکیده
منابع مشابه
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Gene therapy has strong potential for treating a variety of genetic disorders, as demonstrated in recent clinical trials. There is unfortunately no scarcity of disease targets, and the grand challenge in this field has instead been the development of safe and efficient gene delivery platforms. To date, approximately two thirds of the 1800 gene therapy clinical trials completed worldwide have us...
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ژورنال
عنوان ژورنال: Human Gene Therapy
سال: 2020
ISSN: 1043-0342,1557-7422
DOI: 10.1089/hum.2020.29120.bca